Rare Disease Consulting
Greater understanding, treatment development and regulatory measures are introduced to encourage innovation in diseases with low prevalence and high unmet need. All of these aspects make it a very exciting time to work on rare disease.
Still, they represent a myriad of specifics that can be particularly challenging, including…
- The knowledge gaps/disease natural history is often poorly understood
- Not adapted standard trial designs
- Sometimes combined with no standardized definition
- The limited standard good practice guidelines
- The lengthy and complicated diagnosis pathway
- Specific regulatory pathways
- The overall lack of awareness
Get the right expertise, at the right time, for a winning market strategy.
We provide disease-specific data and insights to help you prioritize assets and pipeline.
Business development and licensing, Epidemiology, Forecasting, Health economics and outcomes research, KOL identification & influence mapping, Patient Preferences, Patient reported outcomes,Patient, physician, payer insights, Portfolio assessments & planning
We provide connected clinical and real-world solutions to optimize clinical trials and prepare you for submission.
Submission & Approval
We generate evidence of your product's safety and effectiveness so you can file with the confidence of a well-defined value proposition for all stakeholders.
We offer consultative approaches to ensure the success of your launch using connected commercial and real-world solutions.
Brand Strategy, Health economics and outcomes research, KOL identification & influence mapping, Market Understanding, Non interventional Studies, Patient, Physician insights, Patient reported outcomes, Patient Preferences, Risk Management Plan, Medical writing
We leverage real-world evidence to expand access through new indications with demonstrated product safety and value.
Also within Health
Clinical Research & Medical Affairs
Data and Analytics